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Ultra Rare, Ultra Challenging: A Multi-Stakeholder Dialogue on N-of-1 and Micro-rare Diseases

June 19, 2025 5pm London Uk time 
 
This event discusses the distinct hurdles faced in the realm of n-of-1 conditions, also known as “micro-rare" diseases where a patient may be one of only a handful, or even unique, in the world with their specific diagnosis. This webinar will unite four diverse voices, including a patient perspective, to explore the complex research, regulatory, and access landscapes that characterize these highly individualized medical journeys. Our expert panel will delve into the innovative strategies and emerging solutions that may offer sustainable pathways forward for developing and delivering personalized treatments to those with the rarest of conditions, fostering a deeper understanding of how we can collectively advance care for unique patients.
 
 
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